Member Type: Large Biotech/Pharmaceutical Companies
bluebird bio is pioneering gene therapy with purpose. From their Cambridge, Mass., headquarters, they’re developing gene therapies for severe genetic diseases and cancer, with the goal that people facing potentially fatal conditions with limited treatment options can live their lives fully. Beyond their labs, they’re working to positively disrupt the healthcare system to create access, transparency and education so that gene therapy can become available to all those who can benefit. They’re putting their care and expertise to work across a spectrum of disorders by researching cerebral adrenoleukodystrophy, sickle cell disease, transfusion-dependent ?-thalassemia and multiple myeloma using three gene therapy technologies: gene addition, cell therapy and (megaTAL-enabled) gene editing.